a pioneering laboratory
in gene therapy

For the last 30 years, Genethon has been a pioneer in gene therapy. The teams at Genethon are to thank for many gene therapy success stories, which today are improving the lives of patients exponentially.

Dedicated to the fight against rare diseases, Genethon has developed unique expertise in the design and development of gene therapy products, as well as their pre-clinical and clinical development. Its work is behind a number of treatments on the market, in clinical trial or at the R&D stage, changing the lives of patients and their families.

With 200 scientists and experts, Genethon continues with its mission, namely to develop treatments that change the lives of patients suffering from rare genetic diseases and to eradicate these pathologies.

Genethon is a not-for-profit organization, created in 1990 by the AFM-Telethon, an association of patients and patient families, thanks to the French Telethon.