Newsletter

Genethon newsletter – 2026 Issue Number 2

Genethon, a unique non-profit gene therapy R&D organization founded by the French Muscular Dystrophy Association (AFM-Telethon), reported clinical trial updates for its best-in-class Duchenne muscular dystrophy (DMD) gene therapy and announced a unique collaboration with a US-based company to improve precision… (read more)

Genethon newsletter – 2026 Issue Number 1

PARIS, FRANCE (January 26, 2026) – Genethon, a unique non-profit gene therapy R&D organization founded by the French Muscular Dystrophy Association (AFM-Telethon), began the new year with an R&D licensing deal for its gene therapy approach to Pompe disease and continues pivotal clinical trials of its… (read more)

Genethon newsletter – 2025 Issue Number 1

PARIS, FRANCE (June 19, 2025) – Genethon, a unique non-profit gene therapy R&D organization founded by the French Muscular Dystrophy Association (AFM-Telethon), and its spin-off Atamyo Therapeutics made significant advances in their gene therapies for multiple rare diseases as highlighted in Genethon’s most recent… (read more)

Genethon newsletter – 2024 Issue Number 2

This last issue of 2024 year highlights several major clinical development and scientific milestones over the past several months for Genethon.
– Positive safety and efficacy results for the gene therapy GNT0004, set it apart from all other (read more)

Genethon newsletter – 2024 Issue Number 1

In this new issue, Frédéric Revah, Genethon’s CEO, reviews the results of gene therapy trial for Duchenne Muscular Dystrophy, sponsored by Genethon at Myology Congress and the advances of the (read more)