2021
Rees, M. et Al. « Making sense of missense variants in TTN-related congenital myopathies » Acta neuropathologica 141, 431-453
Andrieu, M. et Al.
« La biosécurité et la cytométrie en flux. In La cytométrie en flux – 2ème édition »
L. Tec&Doc, ed., Chapter 29, pp. 483-492
Galibert, L. et Al.
« Monobac System-A Single Baculovirus for the Production of rAAV »
Microorganisms 9
Shi X. et Al.
« Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients »
Molecular therapy Methods & clinical development 20, 287-297
Barbon, E. et Al.
« Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor »
Gene therapy
