Gene therapy
News
March 6, 2023
Crigler-Najjar Syndrome: Genethon obtains PRIME priority drug status from the EMA for its gene therapy
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February 24, 2023
Chronic septic granulomatosis: biomarkers predict the efficacy of gene therapy
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February 7, 2023
"We made important achievements in 2022 but we still face key challenges in the year ahead"
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January 10, 2023
Genethon Launches Pivotal Clinical Trial of Gene Therapy for Crigler-Najjar Syndrome, a Rare Liver Disease
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December 14, 2022
Publication: Genethon helps clarify a molecular mechanism of mitochondrial malfunction in Duchenne muscular dystrophy
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November 21, 2022
Téléthon 2022: Benjamin, a hope for families thanks to clinical trials
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November 21, 2022
Téléthon 2022 : Benjamin, l’espoir des familles grâce aux essais cliniques
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November 21, 2022
Telethon 2022: for Lucie, "a real opportunity, thanks to advances in research"
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October 11, 2022
Genethon’s Latest Research, Including Advances in Gene Editing and AAV Delivery Vectors for Gene Therapy, to be Featured at European Society for Gene and Cell Therapy, Oct. 11-14, 2022
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October 5, 2022
Publication: Genethon helps identify two vectors optimized for muscles via a European H2020 program
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September 26, 2022
First Patient Dosed in Phase 1/2 Clinical Trial in Europe of Gene Therapy for LGMD-R9
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September 12, 2022
Genethon to Present Its Latest Gene Therapy Research Advancements in Neuromuscular Diseases at the International Myology 2022 Congress
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July 15, 2022
Anne Galy receives the WAS Foundation Callahan Award for her work on Wiskott-Aldrich syndrome
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July 8, 2022
Sickle-cell anemia: a project involving the Gene editing team has just secured European funding
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May 16, 2022
La R&D de Généthon à l'honneur dans plusieurs présentations à la réunion annuelle de l'American Society of Cell & Gene Therapy du 16 au 19 mai 2022, à Washington, DC
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May 16, 2022
Genethon’s R&D to be Featured in Multiple Presentations at ASGCT Annual Meeting, May 16-19
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April 27, 2022
Myopathies des ceintures : I-Stem et Généthon identifient une combinaison pharmacologique pour traiter l'alpha-sarcoglycanopathie
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April 4, 2022
Genethon Joins U.S. Bespoke Gene Therapy Consortium Dedicated to Finding Treatments for Ultra-Rare Diseases
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Serving the public interest
Our mission: Conception, clinic and preclinic development of drugs of genic therapy for rare diseases
Our goal: Providing these innovative treatments to the sick
