Gene therapy
Serving the public interest
Our mission: Conception, clinic and preclinic development of drugs of genic therapy for rare diseases
Our goal: Providing these innovative treatments to the sick
Our science
News
May 16, 2022
La R&D de Généthon à l'honneur dans plusieurs présentations à la réunion annuelle de l'American Society of Cell & Gene Therapy du 16 au 19 mai 2022, à Washington, DC
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May 16, 2022
Genethon’s R&D to be Featured in Multiple Presentations at ASGCT Annual Meeting, May 16-19
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April 4, 2022
Genethon Joins U.S. Bespoke Gene Therapy Consortium Dedicated to Finding Treatments for Ultra-Rare Diseases
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February 28, 2022
Gene Therapies Continue to Emerge as Effective Treatments for Rare Diseases, But Complex Challenges Remain
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February 10, 2022
Genethon’s Lentiviral Vector-Based Gene Therapy Demonstrates Long-Term Safety and Efficacy for Wiskott-Aldrich Syndrome
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January 6, 2022
Genethon Announces Publication of Results paving the way for Gene Therapy for XLH, a Skeletal Disorder
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October 20, 2021
Genethon Presents Significant Advances in Gene Therapy at European Society for Gene and Cell Therapy, Oct 19-22, 2021
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June 28, 2021
Preliminary results of clinical trial for rare liver disease Crigler-Najjar syndrome presented at ESGCT congress
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April 23, 2021
Genethon announces First Patient dosed in Clinical Trial of Investigational Gene therapy GNT 0004 for Duchenne Muscular Dystrophy
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February 28, 2021
Genethon, 30 years of pioneering research and innovation in treating rare diseases
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February 10, 2021
Genethon and WhiteLab Genomics join forces to enhance gene therapy through artificial intelligence
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February 3, 2021
Genethon is delighted about the launch of a gene therapy clinical trial for late-onset Pompe disease
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December 2, 2020
Genethon gets the green light from the ANSM to start an innovative gene therapy trial for Duchenne muscular dystrophy
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September 21, 2020
Genethon welcomes the submission to EMA of Marketing Authorisation Application for LUMEVOQ® Gene Therapy to Treat Vision Loss due to Leber Hereditary Optic Neuropathy (LHON)
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June 10, 2020
A Genethon team succeeds in inhibiting the immune response linked to AAV, opening up the possibility of treating more patients by gene therapy
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January 30, 2020
Genethon welcomes the conclusive results of a gene therapy trial in Chronic Septic Granulomatosis, a rare disease of the immune system
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January 9, 2020
Genethon strengthens its collaboration with Sarepta Therapeutics for the development of the gene therapy product GNT0004 in Duchenne muscular dystrophy
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September 9, 2019
A gene therapy based clinical trial for Fanconi anemia patients offers its first successful results
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June 26, 2019
First in vivo proof-of-concept in Steinert’s myotonic dystrophy, a neuromuscular disease
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May 24, 2019
Towards a clinical trial for gamma-sarcoglycanopathy, limb-girdle muscular dystrophy
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