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Author: admin

Duchenne Muscular Dystrophy: Genethon presents Two-Year consolidated results of the GNT0004 Gene Therapy

May 17, 2025

Genethon Presents Two Year Consolidated Results of Its Gene Therapy Trial for Duchenne Muscular Dystrophy: Maintenance of Motor Functions and Significant, Sustained Reduction in CPK Levels in Patients Treated at the Effective Dose at ASGCT 2025

May 17, 2025

New advances in the treatment of ALS: Genethon’s DNA bank involved in the trial

May 16, 2025

GenoTher Summit 2025: a key event to shape the future of gene therapy

May 15, 2025

Genethon arrives in force at ASGCT 2025 with 12 communications, including 5 oral presentations

May 13, 2025

Genethon Celebrates Rare Disease Day by Highlighting New Technologies to Advance Gene Therapies and Bring Hope to Millions of Patients Worldwide

February 27, 2025

Genethon and Eukarÿs announce a strategic partnership to develop a breakthrough technology to reduce the biomanufacturing cost of gene therapies

January 23, 2025

Ana Buj Bello, winner of the Léon Baratz Prize, Docteur Darolles for her research on a gene therapy to cure myotubular myopathy

December 19, 2024

Genethon newsletter – 2024 Issue Number 2

December 18, 2024

Long-term success of gene therapy in patients with Fanconi anemia

December 17, 2024

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