Publication – Page 33 – Généthon

Forelimb Treatment in a Large Cohort of Dystrophic Dogs Supports Delivery of a Recombinant AAV for Exon Skipping in Duchenne Patients.

February 19, 2021

Atypical phenotypes in titinopathies explained by second titin mutations.

February 19, 2021

Different protein composition and functional properties of adeno-associated virus-6 vector manufactured from the culture medium and cell lysates.

February 19, 2021

A dystrophic muscle broadens the contribution and activation of immune cells reacting to rAAV gene transfer.

February 19, 2021

Acute effect of androgens on maximal force-generating capacity and electrically evoked calcium transient in mouse skeletal muscles.

February 19, 2021

Gait characteristics in a canine model of X-linked myotubular myopathy.

February 19, 2021

Assessment of DNA encapsulation, a new room-temperature DNA storage method.

February 19, 2021

Immunization of Mice with Lentiviral Vectors Targeted to MHC Class II+ Cells Is Due to Preferential Transduction of Dendritic Cells In Vivo.

February 19, 2021

Liver-specific transcriptional modules identified by genome-wide in silico analysis enable efficient gene therapy in mice and non-human primates.

February 19, 2021

Gene therapy prolongs survival and restores function in murine and canine models of myotubular myopathy.

February 19, 2021