Gene replacement rescues severe muscle pathology and prolongs survival in myotubularin-deficient mice and dogs.
2015
Childers, M. K., A. H. Beggs, et al. (2015).
Ann Transl Med 3(17): 257.
2015
Childers, M. K., A. H. Beggs, et al. (2015).
Ann Transl Med 3(17): 257.