Publication – Page 52 – Généthon

C-terminal titin deletions cause a novel early-onset myopathy with fatal cardiomyopathy

February 19, 2021

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients

February 19, 2021

Guidance on Good Cell Culture Practice. A report of the second ECVAM task force on Good Cell Culture Practice – Proceedings of the 19th ESACT Meeting, Harrogate, UK, June 5-8, 2005

February 19, 2021

Ins and outs of therapy in limb girdle muscular dystrophies

February 19, 2021

Amphiphilic Poly[(propylene glycol)-block-(2-methyl-2-oxazoline)] Copolymers for Gene Transfer in Skeletal Muscle

February 19, 2021

Combination of quantification and observation methods for study of ”side population” cells in their “in vitro” microenvironment.

February 19, 2021

Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63 % of patients with Duchenne muscular dystrophy

February 19, 2021

Restoration of Human Dystrophin Following Transplantation of Exon-Skipping-Engineered DMD Patient Stem Cells into Dystrophic Mice

February 19, 2021

AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not alpha-sarcoglycan deficiency

February 19, 2021

Control of beta-cell differentiation by the pancreatic mesenchyme

February 19, 2021