• Who we are?
    • Our history
    • Board of Directors
    • The Management committee and scientific leadership
    • Our scientific advisory board
  • Our research teams
    • Our research teams and our platforms
      • Progressive muscular dystrophies
      • Neuromuscular diseases and gene therapy
      • Gene Editing
      • Immunology and liver diseases
      • DNA Bank
      • Genethon’s Imaging Cytometry Platform
    • Gene Editing
    • Bioproduction
    • Understanding gene therapy
    • Immunology of gene transfer: a crucial issue
  • Our pipeline
    • Duchenne muscular dystrophy
    • Infant Spinal muscular atrophy
    • SMA-PME and Farber’s disease
    • Myotubular myopathy
    • Limb girdle muscular dystrophies
    • Wiskott-Aldrich syndrome
    • Fanconi’s anemia
    • Sickle cell disease
    • Chronic septic granulomatosis
    • Severe Combined Immunodefiency (SCID)
    • Cori Forbes disease
    • GSD1a – Glygogen Storage Disease Type 1a
    • Crigler-Najjar syndrome
    • Pompe disease
    • Leber Hereditary Optic Neuropathy
  • Our partners
  • Our commitment
    • Why work at Genethon?
    • Tours of Genethon
    • 1,000 researchers initiative
    • The DNA School
  • Newsroom
    • News
    • Press Releases
    • Newsletter
    • Publications
Contact Join us

Archives: Publication

Diverse genomic integration of a lentiviral vector developed for the treatment of Wiskott-Aldrich syndrome

February 19, 2021

Dok-4 is a novel negative regulator of T cell activation

February 19, 2021

Real-time monitoring of cell transplantation in mouse dystrophic muscles by a secreted alkaline phosphatase reporter gene

February 19, 2021

CYP7B1 mutations in pure and complex forms of hereditary spastic paraplegia type 5

February 19, 2021

Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons

February 19, 2021

Quantitative proteomic analysis of lentiviral vectors using two dimensional gel electrophoresis

February 19, 2021

Human alpha-Iduronidase Gene Transfer Mediated by Adeno-Associated Virus Types 1, 2, and 5 in the Brain of Nonhuman Primates: Vector Diffusion and Biodistribution

February 19, 2021

Analysis of growth factor expression in affected and unaffected muscles of oculo-pharyngeal muscular dystrophy (OPMD) patients: A pilot study

February 19, 2021

Growth Factor Delivery Approaches in Hydrogels

February 19, 2021

Genetic inactivation of acetylcholinesterase causes functional and structural impairment of mouse soleus muscles

February 19, 2021

Posts navigation

Older posts
Newer posts
Contact Join us Personal data protection policy

Genethon is a member of the Biotherapies Institute for Rare Diseases that was created by AFM-Telethon

AFM-Téléthon
Biotherapies Institute
Genethon
Institute of Myology
I-Stem
En cliquant sur « Tout accepter », vous consentez au dépôt de cookies sur votre appareil pour améliorer votre navigation sur le site, mesurer les performances du site, personnaliser le contenu ou la publicité affichée sur le site et d’autres sites. Votre consentement est valable 6 mois. Vous pouvez personnaliser vos choix ou retirer votre consentement à tout moment en cliquant sur le lien « Gérer mes cookies ». Pour plus d’information, et notamment pour consulter la liste des tiers intervenant sur notre site, consultez la Politique de cookies accessible en bas de page.
Manage my cookies Deny all cookies Accept all
Manage consent

Manage consent

This website uses cookies to improve your experience while you navigate through the website. Out of these cookies, the cookies that are categorized as necessary are stored on your browser as they are essential for the working of basic functionalities of the website. We also use third-party cookies that help us analyze and understand how you use this website. These cookies will be stored in your browser only with your consent. You also have the option to opt-out of these cookies. But opting out of some of these cookies may have an effect on your browsing experience.

Necessary
Always Enabled
Necessary cookies are absolutely essential for the website to function properly. These cookies ensure basic functionalities and security features of the website, anonymously.
Functional
Functional cookies help to perform certain functionalities like sharing the content of the website on social media platforms, collect feedbacks, and other third-party features.
Performance
Performance cookies are used to understand and analyze the key performance indexes of the website which helps in delivering a better user experience for the visitors.
Analytics
Analytical cookies are used to understand how visitors interact with the website. These cookies help provide information on metrics the number of visitors, bounce rate, traffic source, etc.
Advertisement
Advertisement cookies are used to provide visitors with relevant ads and marketing campaigns. These cookies track visitors across websites and collect information to provide customized ads.
Others
Other uncategorized cookies are those that are being analyzed and have not been classified into a category as yet.
Save & Accept
Powered by CookieYes Logo