Publication – Page 41 – Généthon

Large-scale manufacture and characterization of a lentiviral vector produced for clinical ex vivo gene therapy application.

February 19, 2021

Baculovirus VP80 protein and the F-actin cytoskeleton interact and connect the viral replication factory with the nuclear periphery.

February 19, 2021

The reverse block copolymer Pluronic 25R2 promotes DNA transfection of skeletal muscle.

February 19, 2021

The c.273+11dup genetic change in the WAS gene is a functionally neutral polymorphism.

February 19, 2021

An initiative to manufacture and characterize baculovirus reference material.

February 19, 2021

Inhibition of activin receptor type IIB increases strength and lifespan in myotubularin-deficient mice.

February 19, 2021

Pre-clinical study of 21 approved drugs in the mdx mouse.

February 19, 2021

Latest developments in the large-scale production of adeno-associated virus vectors in insect cells toward the treatment of neuromuscular diseases.

February 19, 2021

Gene therapy for the Wiskott-Aldrich syndrome.

February 19, 2021

Quantification of lentiviral vector copy numbers in individual hematopoietic colony-forming cells shows vector dose-dependent effects on the frequency and level of transduction.

February 19, 2021