Publication – Page 32 – Généthon

Proteomics profiling of urine reveals specific titin fragments as biomarkers of Duchenne muscular dystrophy.

February 19, 2021

Repairing without cutting: a safer alternative to gene correction?

February 19, 2021

Cis-splicing and Translation of the Pre-Trans-splicing Molecule Combine With Efficiency in Spliceosome-mediated RNA Trans-splicing.

February 19, 2021

Myostatin is a key mediator between energy metabolism and endurance capacity of skeletal muscle.

February 19, 2021

Long-term safety and efficacy of factor IX gene therapy in hemophilia B.

February 19, 2021

Genome-wide analysis of alpharetroviral integration in human hematopoietic stem/progenitor cells.

February 19, 2021

Forelimb Treatment in a Large Cohort of Dystrophic Dogs Supports Delivery of a Recombinant AAV for Exon Skipping in Duchenne Patients.

February 19, 2021

Differential Muscle Hypertrophy Is Associated with Satellite Cell Numbers and Akt Pathway Activation Following Activin Type IIB Receptor Inhibition in Mtm1 p.R69C Mice.

February 19, 2021

Serum Profiling Identifies Novel Muscle miRNA and Cardiomyopathy-Related miRNA Biomarkers in Golden Retriever Muscular Dystrophy Dogs and Duchenne Muscular Dystrophy Patients.

February 19, 2021

Concurrent measures of fusion and transduction efficiency of primary CD34+ cells with human immunodeficiency virus 1-based lentiviral vectors reveal different effects of transduction enhancers.

February 19, 2021