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Archives: Publication

High urinary ferritin reflects myoglobin iron evacuation in DMD patients.

February 19, 2021

Gene Therapy for Sickle Cell Disease: A Lentiviral Vector Comparison Study.

February 19, 2021

Subretinal Injection of HY Peptides Induces Systemic Antigen-Specific Inhibition of Effector CD4(+) and CD8(+) T-Cell Responses.

February 19, 2021

Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression.

February 19, 2021

Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell Disease.

February 19, 2021

Interactions between Retroviruses and the Host Cell Genome.

February 19, 2021

Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency.

February 19, 2021

Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity.

February 19, 2021

Conceptual Challenges of the Systemic Approach in Understanding Cell Differentiation.

February 19, 2021

Congenital Titinopathy: Comprehensive characterization and pathogenic insights.

February 19, 2021

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