Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients
2007
Charrier, S., Dupre, L., Scaramuzza, S., Jeanson-Leh, L., Blundell, M.P., Danos, O., Cattaneo, F., Aiuti, A., Eckenberg, R., Thrasher, A.J., Roncarolo, M.G. and Galy, A.:
Gene Ther 14 (2007) 415-28.
