Exon-specific U1 snRNAs improve ELP1 exon 20 definition and rescue ELP1 protein expression in a familial dysautonomia mouse model.
2018
Donadon, I., et al. (2018).
Hum Mol Genet 27(14): 2466-2476.
2018
Donadon, I., et al. (2018).
Hum Mol Genet 27(14): 2466-2476.
