Who we are?
Our research teams
Our pipeline
Our partners
Our commitment
Join us
Newsroom

Contact Jobs

Death following high-dose AAV9 gene therapy in a patient with advanced SMA-PME.

2026

Boespflug-Tanguy, O

Mol Ther.

Contact Join us Personal data protection policy

Genethon is a member of the Biotherapies Institute for Rare Diseases that was created by AFM-Telethon

Biotherapies Institute

Institute of Myology

En cliquant sur « Tout accepter », vous consentez au dépôt de cookies sur votre appareil pour améliorer votre navigation sur le site, mesurer les performances du site, personnaliser le contenu ou la publicité affichée sur le site et d’autres sites. Votre consentement est valable 6 mois. Vous pouvez personnaliser vos choix ou retirer votre consentement à tout moment en cliquant sur le lien « Gérer mes cookies ». Pour plus d’information, et notamment pour consulter la liste des tiers intervenant sur notre site, consultez la Politique de cookies accessible en bas de page.
Manage my cookies Deny all cookies Accept all

Manage consent

Manage consent

This website uses cookies to improve your experience while you navigate through the website. Out of these cookies, the cookies that are categorized as necessary are stored on your browser as they are essential for the working of basic functionalities of the website. We also use third-party cookies that help us analyze and understand how you use this website. These cookies will be stored in your browser only with your consent. You also have the option to opt-out of these cookies. But opting out of some of these cookies may have an effect on your browsing experience.

Necessary

Necessary

Always Enabled

Necessary cookies are absolutely essential for the website to function properly. These cookies ensure basic functionalities and security features of the website, anonymously.

Functional

fonctionnel

Functional cookies help to perform certain functionalities like sharing the content of the website on social media platforms, collect feedbacks, and other third-party features.

Performance

performance-fr

Performance cookies are used to understand and analyze the key performance indexes of the website which helps in delivering a better user experience for the visitors.

Analytics

analytique

Analytical cookies are used to understand how visitors interact with the website. These cookies help provide information on metrics the number of visitors, bounce rate, traffic source, etc.

Advertisement

publicite

Advertisement cookies are used to provide visitors with relevant ads and marketing campaigns. These cookies track visitors across websites and collect information to provide customized ads.

Others

autres

Other uncategorized cookies are those that are being analyzed and have not been classified into a category as yet.

Save & Accept

Powered by