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Archives: Publication

Selecting Novel Retino-tropic AAV Capsids by Directed Evolution.

October 16, 2026

Rapamycin nanoparticles mitigate anti-AAV antibody formation in a mouse model of ornithine transcarbamylase deficiency.

October 16, 2026

Capsid stabilization reprograms the nuclear fate of the HIV genome.

October 16, 2026

Promises of co-stimulatory inhibition for durable and repeatable AAV gene therapy.

October 16, 2026

CD8 T-cell activation occurs 24 hours post-AAV administration and is driven by muscle promoter specificity.

October 16, 2026

Post-transplant alloimmune liver disease in bile salt export pump deficiency: A multicenter study

October 16, 2026

DAB2 in LGMD R2: a molecular link between disease progression and lipid dysregulation

October 16, 2026

Flunarizine changes microRNA expression in cell cultures and in a mouse model of spinal muscular atrophy

October 16, 2026

Illuminating “the dark side of the HBB”: Visualizing the full spectrum of Cas9 outcomes.

July 17, 2026

2D Multimodal Image Collection for Fluorescence Prediction from Transmitted Light Microscopy.

July 17, 2026

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